Baseline laboratory evaluation
CBC with WBC differential and reticulocyte count
Hemoglobin F measurement
Renal and liver function tests
Pregnancy test
Counseling
Women and men taking hydroxyurea should use contraception.
Dosage modification is required to optimize opportunity for clinical response and avoid complications from myelotoxicity.
Monitoring
Blood counts at frequent intervals early in therapy and when dosage changes
Periodic renal and liver function tests
Hemoglobin F levels and red blood cell MCV values to detect a biologic response (i.e., an increase in these parameters)
Patient compliance
Dosage escalation end points
Reduction in sickle cell pain frequency and/or severity
A treatment period of six months may be needed to assess response in patients who continue to have symptoms.
If lack of clinical response: (1) myelotoxicity that defines the maximum tolerated dosage for the patientor (2) maximum dosage of 35 mg per kg per day